Intrathecal administration of recombinant human N-acetylgalactosamine 4-sulfatase to a MPS VI patient with pachymeningitis cervicalis
Rojas, Maria Verónica Muñoz; Horovitz, Dafne Dain Gandelman; Jardim, Laura Bannach; Raymundo, Marcia; Llerena Junior, Juan Clinton; Magalhães, Tatiana de Sá Carneiro Pacheco de; Vieira, Taiane Alves; Kakkis, Emil; Giugliani, Roberto (Academic Press, 2013)